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Key Stock Data
The current last sale of $1.24 is 22.77% Higher than the 52 week low.
|Intraday||Last 52 Weeks|
|High:||$ 1.2863||$ 2.65|
|Low:||$ 1.21||$ 1.01|
Company Description (as filed with the SEC)
We are a clinical stage biopharmaceutical company with an emphasis on identifying the genetic drivers of disease and applying this understanding to the pursuit of differentiated novel therapies primarily for pediatric onset, life-altering diseases, including rare and orphan diseases. We look to find treatments for genetically defined diseases for which there are limited therapeutic options currently available, with a primary focus on pediatric patients. This strategy begins with identifying and genetically validating a therapeutic target and using genomics to guide product development. The strategy also involves identifying and acquiring otherwise abandoned or overlooked drug candidates and matching targets and mechanisms of action to novel genetic discoveries. We have partnered with the Center for Applied Genomics, or CAG, at The Children's Hospital of Philadelphia, or CHOP, to implement a genomic medicine driven approach to drug development. ... More ...
Nasdaq Official Price
Jun. 15, 2018
Jun. 15, 2018