(RTTNews) - CRISPR Therapeutics AG (CRSP), which is down more than 20% from its yearly high of $74, recorded last December, expects 2020 to have the potential to be a pivotal year in the company's growth.
CRISPR Therapeutics is a gene editing company developing gene-based medicines for serious diseases using its proprietary CRISPR/Cas9 platform.
The Company's lead investigational program is CTX001 in phase I/II trials in ß-thalassemia and sickle cell disease.
Last November, CRISPR Therapeutics and its partner Vertex announced positive, interim data from the first two patients with severe hemoglobinopathies - one patient with transfusion-dependent beta-thalassemia (TDT) and one patient with severe sickle cell disease (SCD) - treated with CTX001 in the ongoing Phase 1/2 CLIMB clinical trials. Enrollment is ongoing in both trials and the companies expect to provide additional data for these programs in 2020.
The other investigational programs in clinical development are:
-- CTX110, under a phase I/II study in subjects with relapsed or refractory B-cell malignancies. -- CTX120, under a phase I study of in subjects with relapsed or refractory multiple myeloma.
The Company expects to conduct clinical trials in five indications and anticipates new data from the immuno-oncology and hemoglobinopathies programs this year.
CRISPR Therapeutics ended the year 2019 with cash and cash equivalents of $943.8 million.
CRSP has traded in a range of $30.53 to $74.00 in the last 1 year. As of this writing, the stock is up 1.58% at $58.66.
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